Latest News for: mps ii

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REGENXBIO Announces Regulatory Update on RGX-121 BLA for MPS II

The Huntsville Item 10 Feb 2026
FDA issues Complete Response Letter for RGX-121 (clemidsogene lanparvovec) for treatment of Mucopolysaccharidosis II (MPS II)REGENXBIO plans to work with FDA on a path forward with the goal of resubmitting the BLA ....
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REGENXBIO Announces Regulatory Update on RGX-121 BLA for MPS II (Form 8-K) (Regenxbio Inc)

Public Technologies 10 Feb 2026
REGENXBIO Announces Regulatory Update on RGX-121 BLA for MPS II • FDA issues Complete Response Letter for RGX-121 (clemidsogene lanparvovec) for treatment of Mucopolysaccharidosis II (MPS II).
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Bilawal highlights significance of politics of reconciliation, calls for opposition to play ‘responsible’ role

Dawn 28 Dec 2025
Bilawal expressed these views while speaking to the media at the inauguration ceremony of the Sindh Institute of Child Health and Neonatology in Larkana ... Action will be taken against you in accordance with the law and Constitution” ... ....
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Immusoft Secures FDA Orphan Drug Designation for ISP-002 in MPS II, a Progressive Lysosomal Storage Disease

Rio Grande Sun 16 Dec 2025
Orphan Drug Designation for MPS II builds on Immusoft's clinical progress in MPS I and supports expansion of its engineered B cell platform across multiple indications ... .
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