The price tags for the two sickle cell therapies in the U.S. are $3.1 million and $2.2 million although costs can vary by country. The process of giving the therapies is just as big a hurdle.

Fulcrum Therapeutics reports promising late-stage data for sickle cell drug pociredir, with notable hemoglobin improvements.

In the 1990s, sickle cell was still inaccurately labelled a Black disease and was overlooked by many health professionals. My mum stood as my advocate, pushing for adequate pain relief and urging ...

For sickle cell, patients’ cells are removed from the body and CRISPR is used to make an edit that turns back on production of fetal hemoglobin, a form of the protein that babies make in the womb.

The only cure for the pain sickle cell disease can cause is a bone marrow transplant or gene therapies like the one commercially approved by the U.S. Food and Drug Administration in December.

I see a lot of adults with sickle cell, and it’s like they are really going through and if you are really going through, then somewhere, you have slipped between the cracks,” Moore said.

Both were diagnosed with sickle cell disease at a young age. “It’s debilitating. It’s a pain that I can’t even describe. It’s a pain that’s not overcome without severe narcotics.

The price tags for the two sickle cell therapies in the U.S. are $3.1 million and $2.2 million although the cost for gene therapies can vary by country.

The only cure for the pain sickle cell disease can cause is a bone marrow transplant or gene therapies like the one commercially approved by the U.S. Food and Drug Administration in December.

“One in every 365 individuals that have Black or African American ancestry are born with sickle cell every year,” she said. Nicole and Kyle want to educate others about the disease this World ...

The only cure for the pain sickle cell disease can cause is a bone marrow transplant or gene therapies like the one commercially approved by the U.S. Food and Drug Administration in December.